Ionis Pharmaceuticals, Inc. is a biotechnology company based in Carlsbad, California, that specializes in discovering and developing RNA-targeted therapeutics. The company has 3 commercially approved medicines: Spinraza (Nusinersen), Tegsedi (Inotersen), and Waylivra (Volanesorsen) and has 4 drugs in pivotal studies: tominersen for Huntington’s disease, tofersen for SOD1-ALS, … Web29 mrt. 2024 · As the leader in RNA-targeted therapeutics for more than three decades, Ionis has focused every moment on advancing drug discovery, development, and providing hope for patients. Our broadly applicable, versatile, and rapidly advancing technology … With RNA as the target that forms the basis of our novel drug discovery platform, we … Dr. Monia is the chief executive officer, a member of the board of directors and a … Our antisense therapies are designed to interact precisely with RNA, allowing us … With patient needs as our central focus, we have become the leader in the discovery … Ionis is focused on delivering RNA-targeted therapeutics with transformational … Ionis is invested in the success of our employees. All of our trainings, ... you’ll … IONIS-MAPT Rx, also known as BIIB080, is an investigational antisense medicine … Ion-ARPA programs will be funded (up to $1M per laboratory) based on high …
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Web3 nov. 2024 · Alnylam and Sanofi have revealed full phase 3 data on their RNA interference (RNAi) drug patisiran, soundly beating a rival candidate from Ionis, inotersen. Both drugs target hereditary... Web17 dec. 2024 · The ASO ION582 is targeting this long noncoding RNA to reactivate expression of a gene that would have been otherwise silenced, Dermeier explains. A trial to study ION582 is listed on the ClinicalTrials.gov registry but has not started yet. There is a growing interest in noncoding RNA, especially in the oncology field. graham flack secretary of the treasury board
New data presented at AD/PD™2024 show IONIS-MAPT Rx …
Web13 dec. 2024 · AOC 1001 aims to deplete DMPK mRNA, releasing the trapped RNA-processing proteins. Biogen and Ionis previously took a stab at DMPK mRNA with the ASO ISIS-DMPK Rx . A phase I/IIa trial hinted at ... Web24 mrt. 2024 · Although there may be no single method used by those developing RNA-targeted drugs, Ionis has advanced many drugs into the clinic and here we highlight … Web18 apr. 2024 · Ionis is developing an in-house and partnered pipeline of RNA-targeted drugs for severe and rare diseases. The company's first approved product, Spinraza™ … china gift ideas 20th wedding anniversary